Bringing any treatment from concept to clinic comes with a unique set of challenges, but rare indications amplify the complexity.
Small patient populations make trial recruitment arduous
Limited natural history data complicates endpoint selection and trial design
Manufacturing specialized therapies on a small scale adds cost and strains logistics
To address these challenges and more, leaders in clinical development, translational science, and advanced therapy manufacturing collected their experiences into a free ungated eBook.
Expert insights from 200 rare disease development programs
Set your study up for success with practical (and actionable) advice:
Rob Maiale is an award-winning creative director with over 15 years of experience developing content and marketing strategies for leading healthcare and pharmaceutical brands. His background spans patient education, clinical development, pharma, medical devices, and a broad range of diagnostic modalities. Rob partners with Precision experts to strategically showcase their knowledge through creative storytelling and engaging content strategies.