
Case Study: Early Genotype Confirmation Rescued a Phase 1-2 SCID Trial
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Discover
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100% sourced from leading minds on the front lines of research
Clinical Trials - Rare Diseases
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Alexis Hobbins-White
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Robert Bauer
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Helen O.
Gavin P.
Kelly L.
Translational Research - Biomarkers
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Deborah P.
Christie .
Translational Research - Regulatory - Assays - Gene Therapies
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Deborah P.
Travis H.
Translational Research - Regulatory - Assays - Gene Therapies
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Deborah P.
Maham A.
Manufacturing - Cell Therapies - Gene Therapies
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Tony K.
Christian H.
Manufacturing - Cell Therapies - Gene Therapies
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Tony K.
Danny F.
Phil M.
Manufacturing - Cell Therapies - Gene Therapies
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Tony Khoury